Scholar Rock Holding Corp

On October 10, 2025, Novo Nordisk informed us that, following the FDA Form 483 issued to Catalent Indiana, LLC (owned by Novo Nordisk) on July 14, 2025, FDA has determined that the inspection classification of this facility is “official action indicated” (OAI). We continue to work closely with Novo Nordisk, and we have requested a Type […] The post Update on Third Party Manufacturing Site appeared first on Scholar Rock.

Hear how members of the SMA community navigate the challenges of living with SMA as they share stories of overcoming adversity, finding strength and embracing hope. The post Believe in What is Possible appeared first on Scholar Rock.

Watch the SMA community as they share their hopes and excitement for the future, fueled by the potential of groundbreaking treatment. These voices are a powerful reminder that the future is brighter than ever as members of the SMA community embrace the promise of progress and a life full of potential. The post A Future Full of Possibilities appeared first on Scholar Rock.

Hear firsthand from members of the SMA community who are pushing past limitations, embracing their abilities, and proving that SMA is just one part of their journey—not the end. These powerful stories remind us that it’s not about what they can’t do—it’s about everything they’re capable of achieving, no matter the challenges. The post Expanding What is Possible appeared first on Scholar Rock.

Scholar Rock recently had the opportunity to speak one-on-one with individuals living with spinal muscular atrophy (SMA) to ask a simple, but powerful question: “What possibilities do you hope to see for those living with SMA?” Their responses—from continuing to play competitive sports, to pursuing a career in musical theater, to living more independently—inspire us […] The post What do new possibilities mean to those living with SMA? appeared first on Scholar Rock.

Scholar Rock recently sat down with the caregivers of loved ones living with spinal muscular atrophy (SMA), who shared their hopes for the future. Their perspectives shed light on the possibilities they envision for their loved ones – from living independently to pursuing fulfilling, passionate careers. Each voice reflects our commitment to championing what matters […] The post Caregiver perspectives on creating possibilities for loved ones living with SMA appeared first on Scholar Rock.